Plasticity of human microglia and brain perivascular macrophages in aging and Alzheimer’s disease
Cite
Lee, D., Vicari, J.M., Porras, C., Spencer, C., Pjanic, M., Wang, X., Kinrot, S., Weiler, P., Kosoy, R., Bendl, J. and Prashant, N.M., 2024. Plasticity of human microglia and brain perivascular macrophages in aging and Alzheimer’s disease. Nat Genet (2026).
https://doi.org/10.1038/s41588-026-02716-6
Abstract
Myeloid cells, including microglia and perivascular macrophages, are central to Alzheimer’s disease (AD) neurobiology, yet their role remains incompletely understood. We profiled 832,505 human myeloid cells from the prefrontal cortex of 1,607 donors spanning the lifespan and showing varying degrees of AD neuropathology. We delineated six subclasses comprising 13 transcriptionally distinct subtypes and identified adaptive changes associated with aging and AD progression. Here we show that a disease-associated microglial subtype, characterized by elevated GPNMB expression and enriched for polygenic AD risk, expands with AD pathology and shows increased phagocytic activity. We identify MITF as an upstream regulator required to maintain this microglial state. Cell–cell interaction analyses prioritize APOE–SORL1 and APOE–TREM2 signaling pairs associated with disease progression. Using human and mouse models, we demonstrate that the neuroprotective effects of this microglial subtype depend on TREM2. These findings provide mechanistic insights into myeloid cell function in aging and AD, aiding therapeutic discovery.
Datasets
1. Fresh ex vivo myeloid single cell RNA-seq from human prefrontal cortex
ExploreSubject ID
Sequencing source
Sample collection method
Sample source
Cell type
Cell type (subclass)
Cell sub type
Disease
CERAD
Braak
Dementia
Assay
Sex
Tissue
Ethnicity
Age group
Age
Sample ID
Sample preservation method
Donor living at sample collection
Reference genome
microglia (MG)502,413 cells perivascular macrophage (PVM)40,599 cells Homeo_PICALM108,413 cells Adapt_TMEM16339,127 cells Alzheimer’s disease (AD)225,855 cells dorsolateral prefrontal cortex543,012 cells European American470,117 cells Hispanic or Latin28,451 cells African American25,570 cells 
2. Frozen in silico sorted myeloid single nuclei RNA-seq from human prefrontal cortex
ExploreRep ID
Pool ID
Sample source
Cell type
Cell type (subclass)
Cell sub type
Assay
Disease
Sex
Tissue
Ethnicity
Age
Age group
Sample preservation method
Donor living at sample collection
Reference genome
NPSAD-20201106-A21,156 cells NPSAD-20201103-C21,074 cells NPSAD-20201208-C21,062 cells NPSAD-20201202-A11,050 cells NPSAD-20201202-C21,047 cells NPSAD-20201106-A1999 cells NPSAD-20201030-A1990 cells NPSAD-20210303-A1984 cells NPSAD-20201209-C2982 cells NPSAD-20210323-A2952 cells NPSAD-20210323-A1933 cells NPSAD-20201028-A2926 cells NPSAD-20201103-A2915 cells NPSAD-20210303-A2911 cells NPSAD-20201124-A1902 cells NPSAD-20201030-A2879 cells NPSAD-20201209-A2878 cells NPSAD-20210113-A1870 cells NPSAD-20201202-C1870 cells NPSAD-20201209-C1848 cells NPSAD-20201124-A2840 cells NPSAD-20201103-A1835 cells NPSAD-20210114-C2818 cells NPSAD-20201028-A1817 cells NPSAD-20201120-C1813 cells NPSAD-20201202-A2809 cells NPSAD-20210113-A2799 cells NPSAD-20201113-C1795 cells NPSAD-20201208-C1791 cells NPSAD-20201113-A2783 cells NPSAD-20201110-A1774 cells NPSAD-20201209-A1770 cells NPSAD-20201214-C1767 cells NPSAD-20201120-A1767 cells NPSAD-20201013-A1762 cells NPSAD-20210120-A1756 cells NPSAD-20201120-A2753 cells NPSAD-20201120-C2750 cells NPSAD-20201113-A1749 cells NPSAD-20201217-C1747 cells NPSAD-20210114-C1742 cells NPSAD-20201218-A1737 cells NPSAD-20201214-C2726 cells NPSAD-20201030-C2721 cells NPSAD-20201204-A1719 cells NPSAD-20201110-A2718 cells NPSAD-20210204-A1715 cells NPSAD-20201117-A2712 cells NPSAD-20201210-A2704 cells NPSAD-20201203-A1703 cells NPSAD-20201217-C2696 cells NPSAD-20201215-C1694 cells NPSAD-20201113-C2691 cells NPSAD-20201218-A2672 cells NPSAD-20201204-A2670 cells NPSAD-20210114-A2670 cells NPSAD-20201210-A1668 cells NPSAD-20201013-A2668 cells NPSAD-20201216-A2667 cells NPSAD-20210122-A1665 cells NPSAD-20201203-A2664 cells NPSAD-20201215-A2664 cells NPSAD-20201208-A1664 cells NPSAD-20201027-A2661 cells NPSAD-20201216-A1651 cells NPSAD-20210211-C2650 cells NPSAD-20201118-A2647 cells NPSAD-20210120-A2645 cells NPSAD-20201103-C1642 cells NPSAD-20210203-C1640 cells NPSAD-20201211-A1636 cells NPSAD-20201125-C1632 cells NPSAD-20201104-C1632 cells NPSAD-20201030-C1629 cells NPSAD-20201029-A1626 cells NPSAD-20210211-C1626 cells NPSAD-20201027-A1625 cells NPSAD-20201118-A1619 cells NPSAD-20201208-A2618 cells NPSAD-20201211-C2613 cells NPSAD-20210119-A2611 cells NPSAD-20201215-A1610 cells NPSAD-20201125-C2605 cells NPSAD-20201204-C1605 cells NPSAD-20210114-A1604 cells NPSAD-20210311-A2601 cells NPSAD-20201106-C2598 cells NPSAD-20201204-C2596 cells NPSAD-20201125-A1585 cells NPSAD-20201125-A2579 cells NPSAD-20201117-C2577 cells NPSAD-20201029-A2576 cells NPSAD-20210311-A1574 cells NPSAD-20201111-C2574 cells NPSAD-20201215-C2574 cells NPSAD-20210119-A1570 cells NPSAD-20201123-C2566 cells NPSAD-20210223-A1566 cells NPSAD-20201221-A1565 cells NPSAD-20210304-A2563 cells NPSAD-20210305-A2558 cells NPSAD-20201216-C1558 cells NPSAD-20210212-C2557 cells NPSAD-20201111-C1555 cells NPSAD-20210305-A1553 cells NPSAD-20201016-A2551 cells NPSAD-20210119-C1550 cells NPSAD-20210126-A1550 cells NPSAD-20201028-C2546 cells NPSAD-20210203-C2530 cells NPSAD-20201112-A2521 cells NPSAD-20201106-C1521 cells NPSAD-20201029-C2521 cells NPSAD-20201105-C2519 cells NPSAD-20201029-C1518 cells NPSAD-20210319-A1513 cells NPSAD-20201020-A1511 cells NPSAD-20210119-C2508 cells NPSAD-20201117-C1506 cells NPSAD-20201112-A1504 cells NPSAD-20210218-A2502 cells NPSAD-20210128-A2501 cells NPSAD-20201211-A2500 cells NPSAD-20210212-C1499 cells NPSAD-20210126-C2497 cells NPSAD-20201105-C1494 cells NPSAD-20201119-A1491 cells NPSAD-20201104-C2490 cells NPSAD-20201028-C1490 cells NPSAD-20210304-A1483 cells NPSAD-20201020-A2483 cells NPSAD-20201119-A2479 cells NPSAD-20201105-A1479 cells NPSAD-20210121-C2473 cells NPSAD-20201216-C2473 cells NPSAD-20210202-C2472 cells NPSAD-20201123-C1468 cells NPSAD-20201022-A1467 cells NPSAD-20210202-C1454 cells NPSAD-20201117-A1451 cells NPSAD-20210121-C1450 cells NPSAD-20210128-A1448 cells NPSAD-20210211-A2448 cells NPSAD-20210319-A2446 cells NPSAD-20201203-C2445 cells NPSAD-20201021-A1445 cells NPSAD-20210120-C1439 cells NPSAD-20210121-A1434 cells NPSAD-20201211-C1433 cells NPSAD-20210310-A2430 cells NPSAD-20210209-A1430 cells NPSAD-20201015-C2427 cells NPSAD-20210129-C1419 cells NPSAD-20210126-C1418 cells NPSAD-20210121-A2417 cells NPSAD-20201022-A2410 cells NPSAD-20210127-A4405 cells NPSAD-20201021-A2401 cells NPSAD-20210310-A1395 cells NPSAD-20201027-C2389 cells NPSAD-20210127-A3384 cells NPSAD-20210120-C2381 cells NPSAD-20210318-A2380 cells NPSAD-20210219-C2371 cells NPSAD-20201203-C1370 cells NPSAD-20210205-A2368 cells NPSAD-20201221-A2368 cells NPSAD-20210302-A1366 cells NPSAD-20201015-C1364 cells NPSAD-20210205-A1358 cells NPSAD-20201110-C1356 cells NPSAD-20201111-A1352 cells NPSAD-20210223-C2351 cells NPSAD-20210302-A2351 cells NPSAD-20210212-A1346 cells NPSAD-20201111-A2345 cells NPSAD-20210126-A2340 cells NPSAD-20201027-C1325 cells NPSAD-20210129-A2321 cells NPSAD-20210212-A2320 cells NPSAD-20201124-C2307 cells NPSAD-20201124-C1307 cells NPSAD-20201016-A1306 cells NPSAD-20201218-C1304 cells NPSAD-20210318-A1300 cells NPSAD-20201105-A2298 cells NPSAD-20210113-C1288 cells NPSAD-20201218-C2287 cells NPSAD-20201110-C2272 cells NPSAD-20201023-A2270 cells NPSAD-20210312-A1267 cells NPSAD-20210218-C2263 cells NPSAD-20210216-C2263 cells NPSAD-20201221-C1260 cells NPSAD-20201221-C2256 cells NPSAD-20210129-A1248 cells NPSAD-20210217-C1238 cells NPSAD-20210223-C1236 cells NPSAD-20201119-C2235 cells NPSAD-20210209-A2235 cells NPSAD-20210122-A2215 cells NPSAD-20201023-A1212 cells NPSAD-20210216-C1208 cells NPSAD-20210218-A1203 cells NPSAD-20210211-A1203 cells NPSAD-20210216-A1196 cells NPSAD-20210216-A2187 cells NPSAD-20210316-A2185 cells NPSAD-20210217-C2184 cells NPSAD-20210217-A2181 cells NPSAD-20210316-A1176 cells NPSAD-20201119-C1157 cells NPSAD-20210127-C2150 cells NPSAD-20210127-C1150 cells NPSAD-20210113-C2138 cells NPSAD-20210204-A2130 cells NPSAD-20210219-C1100 cells NPSAD-20210217-A114 cells NPSAD-20210312-A214 cells NPSAD-20210218-C110 cells microglia (MG)252,098 cells perivascular macrophages (PVM)37,395 cells Homeo_PICALM105,686 cells Adapt_TMEM16312,509 cells 10x 3' v3, single-nucleus289,493 cells Alzheimer disease85,697 cells central nervous system disorder61,284 cells schizophrenia21,163 cells Alzheimer disease || Lewy body dementia20,483 cells vascular dementia || Alzheimer disease8,626 cells bipolar disorder6,665 cells Parkinson disease5,016 cells Lewy body dementia4,123 cells Alzheimer disease || schizophrenia2,562 cells dorsolateral prefrontal cortex289,493 cells European American200,534 cells African American54,302 cells Hispanic or Latin18,232 cells Native American1,076 cells 
Alias names
syn52795287, PsychAD